Tag: #RareDiseases

What is Granulomatosis with Polyangiitis Disease, its Symptoms, Causes and Prevention

Recently in Banglore, a seven-year-old girl was diagnosed with Granulomatosis with Polyangiitis or GPA, also known as Wegener's Granulomatosis,...

FDA Approves First Treatment for Rare, Life-Threatening Genetic Disorder

The FDA has granted approval for the first-ever treatment targeting Niemann-Pick disease type C (NPC), a rare genetic disorder...